Liver specific delivery of messenger RNA
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Accused Products
Abstract
Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.
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Citations
1 Claim
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1. The cationic lipid:
Specification