Agents for Treating Diseases Caused by Nonsense Mutations
First Claim
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1. A composition comprising a dipeptide antibiotic for treating a disease caused by a nonsense mutation.
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Abstract
The present invention comprises compositions for treating diseases caused by nonsense mutations, including dipeptide antibiotics of Formula (I) shown below, such as negamycin. Unlike aminoglycoside antibiotics such as gentamicin, dipeptide antibiotics can induce the expression of mature proteins by readthrough nonsense mutations without generating serious side effects.
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3 Claims
- 1. A composition comprising a dipeptide antibiotic for treating a disease caused by a nonsense mutation.
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